Gene therapies involving targeted delivery routes of administration require many considerations for successful preclinical development. This session will review the complexities of targeted administration including MRI-guided delivery. The session will also review the regulatory perspectives supporting study designs and the specialized study logistics, techniques and endpoints unique to these programs.

 

Presenters

Shawna M. Jackman, PhD, DABT
Sr. Principal Research Scientist

Barak Gunter, PhD
Sr. Research Scientist