Gene therapies involving targeted delivery routes of administration require many considerations for successful preclinical development. This session will review the complexities of targeted administration including MRI-guided delivery. The session will also review the regulatory perspectives supporting study designs and the specialized study logistics, techniques and endpoints unique to these programs.

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Shawna M. Jackman, PhD, DABT
Sr. Principal Research Scientist

Barak Gunter, PhD
Sr. Research Scientist